Examples of Diseases that Utilize Gene‐Based Therapy

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Overview / Abstract:

Target Audience

This activity is intended for primary care providers, internal-medicine specialists, pediatricians, pulmonologists, cardiologists, endocrinologists, gastroenterologists, hepatologists, neurologists, neuromuscular specialists, infectious-disease specialists, obstetricians/gynecologists, rheumatologists, dermatologists, hematologists, oncologists, neonatologists, genetic counselors, social workers, psychologists, nurse practitioners, physician assistants, nurses, and pharmacists

Learning Objectives

Upon completion of this activity, participants should be better able to:

Cite evidence for the use of gene‐based therapies that are approved or pending approval for the management of medical disorders
Counsel patients about clinical‐trial opportunities

Expiration

Apr 29, 2022

Discipline(s)

Nursing CNE, Pharmacy CPE, Physician CME, Physician Assistant CME

Format

Online

Credits / Hours

1.0 AMA PRA Category 1 Credit(s)™

Accreditation

ACCME

Presenters / Authors / Faculty

Faculty

Alessandra Biffi, MD
Professor of Pediatrics
Director, Division of Pediatric Hematology,
Oncology and Stem Cell Transplant
University of Padua

Kevin Flanigan, MD
Director, Center for Gene Therapy
Robert F. & Edgar T. Wolfe Foundation
Endowed Chair in Neuromuscular Research
Director, Nationwide Children’s Hospital
Center for Research Translation in Muscular Dystrophy
Therapeutic Development
Abigail Wexner Research Institute Nationwide Children’s Hospital
Professor of Pediatrics and Neurology
The Ohio State University

Kimberly Goodspeed, MD
Assistant Professor of Pediatrics,
Neurology Division
University of Texas Southwestern Medical
Center Dallas

Stephan A. Grupp, MD, PhD
Section Chief, Cellular Therapy and Transplant
Director, Cancer Immunotherapy Program
Children’s Hospital of Philadelphia
Novotny Professor of Pediatrics
Perelman School of Medicine at the
University of Pennsylvania

John Kessler, MD
Davee Professor
Davee Department of Neurology
Northwestern University

Julie A. Parsons, MD
Haberfeld Family Endowed Chair in
Pediatric Neuromuscular Disorders
Professor of Clinical Pediatrics and Neurology
University of Colorado School of Medicine
Children's Hospital Colorado

Perry B. Shieh, MD, PhD, FAAN
Professor of Neurology and Pediatrics
David Geffen School of Medicine at UCLA
University of California, Los Angeles

Sponsors / Supporters / Grant Providers

Astellas Gene Therapies; AVROBIO, Inc.; Biogen; CRISPR Therapeutics, Inc.; Helixmith Co., Ltd; Orchard Therapeutics; REGENXBIO Inc.; and uniQure, Inc.

Keywords / Search Terms

Relias LLC Relias LLC., FreeCME., Rare Disorders Free CE CME

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