Overview / Abstract: |
TARGET AUDIENCE STATEMENT OF NEED/PROGRAM OVERVIEW You are invited to join us for an educational activity designed to review the efficacy and safety data on new therapeutic strategies for GSD1a, as well as the rationale for gene therapy and its ability to transcend the limitations of the standard-of-care. Led by a clinical geneticist and a hepatologist, “Can Gene Therapy Transform the Lives of Patients with GSD1a?”, will discuss the diagnosis and differentiation of GSD1a from other GSD types, review the limitations of dietary regulation and transplantation, and describe the mechanisms of action, benefits, and risks associated with emerging gene therapies. This activity will also help clinicians anticipate and mitigate treatment-related adverse events. EDUCATIONAL OBJECTIVES |
Expiration |
Apr 06, 2024 |
Discipline(s) |
Physician CME |
Format |
Online |
Credits / Hours |
1.0 |
Accreditation |
ACCME |
Presenters / Authors / Faculty |
David F. Rodriguez- Buritica, MD |
Sponsors / Supporters / Grant Providers |
Ultragenyx |
Keywords / Search Terms |
Relias LLC Relias LLC; FreeCME; Free CME; Gene Therapy FreeCME; GSD1a CME Free CE CME |